Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
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Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
A systematic review of quality of life in sickle cell disease and thalassemia after stem cell transplant or gene therapy - ScienceDirect
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Β-Thalassemias | NEJM
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect
Frontiers | New Insights Into Pathophysiology of β-Thalassemia
IJMS | Free Full-Text | Iron Overload and Chelation Therapy in Non-Transfusion Dependent Thalassemia
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PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar
Cureus | Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Thalassaemia - The Lancet
Recent Progress in Gene Therapy and Other Targeted Therapeutic Approaches for Beta Thalassemia | Bentham Science
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
